Tuesday, November 4
8:00 am Check-In & Coffee
WORKSHOP A: 9am
Creating a Patient Advocacy Playbook That Works: Practical Strategies from Preclinical to Post-Trial
Synopsis
This workshop brings together patient advocacy leaders, recruitment and engagement specialists, clinical operations, and medical affairs teams to collaboratively define what effective advocacy partnerships look like at every stage of the drug development journey. Through real-world case studies and facilitated group exercises, we’ll begin shaping a reusable resource to guide teams in embedding transparency, trust, and meaningful patient partnership – well before recruitment begins and long after the trial ends.
This workshop will gather experts to:
- Define best practices for engaging patient advocacy groups from preclinical to post commercial phases
- Discuss crowdsourcing lessons learned on what’s worked, and what hasn’t, across multiple companies and trials
- Co-create a practical take-home guide to support long-term, consistent advocacy partnerships across the industry
12:00 pm Lunch & Networking
WORKSHOP B: 1pm
Embedding Digital Tools & AI Across Rare Disease Trials to Support Access, Recruitment & Real-World Evidence
Synopsis
This interactive workshop will explore how rare disease teams are moving beyond recruitment acceleration to integrate AI, digital platforms, and RWE strategies across trial planning, execution, and post-trial access. With fragmented populations, lengthy diagnoses, and limited clinical precedent, sponsors must build smarter, more connected trial strategies – balancing recruitment with evidence quality, feasibility, and downstream access needs. Through case-based group exercises and discussion, this session will explore how sponsors are using AI-informed platforms, digital outreach, and real-world data to drive trial readiness, patient-centricity, and long-term value.
This workshop will gather experts to discuss:
- Operationalising digital tools across patient journey mapping, site readiness, and feasibility to support smarter, more inclusive trial planning
- Balancing recruitment and evidence needs by integrating real-world data and digital endpoints that support both trial success and downstream regulatory/payer engagement
- Enabling access beyond the trial with platforms that support early identification, evidence generation, and smoother transitions to early access orpost-trial programs
- Cross-functional collaboration to embed AI and digital strategies that meet the needs of medical, access, and clinical teams from day one