In the face of unprecedented cost-per-patient expenses, the FDA’s recent focus on rare disease, and a myriad of options for identifying, engaging, screening, and retaining eligible patients, it is essential to prioritize patient-centric recruitment strategies. As the landscape of rare disease research undergoes a transformative shift, by placing the patient at the heart of recruitment efforts, we can effectively address the significant unmet medical needs in rare diseases and streamline the pathway to innovative treatments.

The Patient Recruitment for Rare Disease Trials Summit served as the premier event for experts in patient recruitment, advocacy and clinical operations to unite in order to navigate cost-efficient, patient centric recruitment to expedite enrolment in rare disease trials. Attendees got the chance to collaborate with industry experts working towards a common goal: ensuring that patients with rare diseases have access to life-changing therapies.