The rare disease trial landscape stands at a pivotal tipping point. While unprecedented advances in trial design, digital tools, and regulatory flexibility are accelerating innovation like never before, the reality for patients remains stark: over 90% of rare diseases still lack an FDA-approved treatment. For many, clinical trials represent the only path to care, yet access remains uneven. Geographic isolation, diagnostic delays, and socioeconomic barriers continue to exclude many patients, especially from underserved communities, from participating in research.

Add to this the small, dispersed patient populations, high protocol complexity, and a shortage of disease-specific expertise, and it’s clear that traditional recruitment approaches no longer suffice.

Now in its second year, the Patient Recruitment for Rare Disease Trials Summit stands as the premier forum dedicated to closing this critical gap. Designed for leaders in Patient Recruitment, Clinical Operations, Patient Advocacy, and Medical Affairs this summit unites innovators reshaping rare disease trial access across the entire patient journey. Over three focused days, you’ll explore cutting-edge strategies spanning early patient identification to decentralized, patient-centric trial models that support participants from diagnosis through to long-term retention. Now is the time to accelerate creative recruitment strategies, deepen early patient engagement, and harness innovative technologies to ensure no rare disease patient is left behind in the race for transformative therapies.