Pharma Thought Leaders:






Biotech Thought Leaders:

Amanda Sowinski
Associate Director, Patient Professional Advocacy & Global Pompe Lead
Amicus Therapeutics









Matt Hay
U.S. Director of Advocacy for Metabolics - Neurofibromatosis (NF) and Hypophosphatasia (HPP)
Alexion Pharmaceuticals



Patient & Advocacy Voices:




Trusted Partners:
