Embedding Digital Tools & AI Across Rare Disease Trials to Support Access, Recruitment & Real-World Evidence
Time: 1:05 pm
day: Pre-Conference Day
Details:
This interactive workshop will explore how rare disease teams are moving beyond recruitment acceleration to integrate AI, digital platforms, and RWE strategies across trial planning, execution, and post-trial access. With fragmented populations, lengthy diagnoses, and limited clinical precedent, sponsors must build smarter, more connected trial strategies – balancing recruitment with evidence quality, feasibility, and downstream access needs. Through case-based group exercises and discussion, this session will explore how sponsors are using AI-informed platforms, digital outreach, and real-world data to drive trial readiness, patient-centricity, and long-term value.
This workshop will gather experts to discuss:
- Operationalising digital tools across patient journey mapping, site readiness, and feasibility to support smarter, more inclusive trial planning
- Balancing recruitment and evidence needs by integrating real-world data and digital endpoints that support both trial success and downstream regulatory/payer engagement
- Enabling access beyond the trial with platforms that support early identification, evidence generation, and smoother transitions to early access orpost-trial programs
- Cross-functional collaboration to embed AI and digital strategies that meet the needs of medical, access, and clinical teams from day one
Speakers:
